# Exploratory Muscle Biopsy Assessment Study in Patients With Late-Onset Pompe Disease Treated With Alglucosidase Alfa

> **NCT01288027** · PHASE4 · COMPLETED · sponsor: **Genzyme, a Sanofi Company** · enrollment: 16 (actual)

## Conditions studied

- Pompe Disease (Late-Onset)
- Glycogen Storage Disease Type II (GSD II)
- Glycogenesis 2 Acid Maltase Deficiency

## Interventions

- **BIOLOGICAL:** Alglucosidase Alfa

## Key facts

- **NCT ID:** NCT01288027
- **Lead sponsor:** Genzyme, a Sanofi Company
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE4
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2011-06
- **Primary completion:** 2013-12
- **Final completion:** 2013-12
- **Target enrollment:** 16 (ACTUAL)
- **Last updated:** 2014-12-19


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01288027

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01288027, "Exploratory Muscle Biopsy Assessment Study in Patients With Late-Onset Pompe Disease Treated With Alglucosidase Alfa". Retrieved via AI Analytics 2026-06-03 from https://api.ai-analytics.org/clinical/NCT01288027. Licensed CC0.

---

*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*