Safety and Efficacy of Olesoxime (TRO19622) in 3-25 Years SMA Patients.
NCT01302600
·
clinicaltrials.gov ↗
PHASE2
Phase
COMPLETED
Status
165
Enrollment
INDUSTRY
Sponsor class
Conditions
Spinal Muscular Atrophy Type II
Spinal Muscular Atrophy Type III Non Ambulant
Interventions
DRUG:
Olesoxime
DRUG:
Placebo
Sponsor
Hoffmann-La Roche
Collaborators
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