Gene Therapy for Fanconi Anemia

NCT01331018 · clinicaltrials.gov ↗

PHASE1

Phase

TERMINATED

Status

3

Enrollment

OTHER

Sponsor class

Stopped Study ended early due to end of funding.

Conditions

Fanconi Anemia

Interventions

PROCEDURE: Bone Marrow Aspiration
BIOLOGICAL: Filgrastim
BIOLOGICAL: Genetically Engineered Hematopoietic Stem Progenitor Cells
OTHER: Laboratory Biomarker Analysis
PROCEDURE: Leukapheresis
DRUG: Methylprednisolone
DRUG: Plerixafor
DRUG: Prednisone

Sponsor

Fred Hutchinson Cancer Center

Collaborators

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