Clinical Study of AAV1-gamma-sarcoglycan Gene Therapy for Limb Girdle Muscular Dystrophy Type 2C

NCT01344798 · clinicaltrials.gov ↗

PHASE1

Phase

COMPLETED

Status

9

Enrollment

OTHER

Sponsor class

Conditions

Limb Girdle Muscular Dystrophy Type 2C
Gamma-sarcoglycanopathy

Interventions

BIOLOGICAL: AAV1-gamma-sarcoglycan vector injection

Sponsor

Genethon