Gene Therapy for Wiskott-Aldrich Syndrome (WAS)
NCT01347242
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
COMPLETED
Status
6
Enrollment
OTHER
Sponsor class
Conditions
Wiskott-Aldrich Syndrome
Interventions
GENETIC:
Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS gene
Sponsor
Genethon
Collaborators
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