# A Retrospective Natural History Study of Patients With Lysosomal Acid Lipase Deficiency/Wolman Phenotype

> **NCT01358370** · — · COMPLETED · sponsor: **Alexion Pharmaceuticals, Inc.** · enrollment: 40 (actual)

## Conditions studied

- Lysosomal Acid Lipase Deficiency
- Wolman Disease

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT01358370
- **Lead sponsor:** Alexion Pharmaceuticals, Inc.
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2010-11
- **Primary completion:** 2013-01
- **Final completion:** 2013-03
- **Target enrollment:** 40 (ACTUAL)
- **Last updated:** 2016-06-27


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01358370

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01358370, "A Retrospective Natural History Study of Patients With Lysosomal Acid Lipase Deficiency/Wolman Phenotype". Retrieved via AI Analytics 2026-06-08 from https://api.ai-analytics.org/clinical/NCT01358370. Licensed CC0.

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