# EPI-743 for Mitochondrial Respiratory Chain Diseases

> **NCT01370447** · — · NO_LONGER_AVAILABLE · sponsor: **PTC Therapeutics**

## Conditions studied

- Mitochondrial Diseases

## Interventions

- **DRUG:** EPI-743

## Key facts

- **NCT ID:** NCT01370447
- **Lead sponsor:** PTC Therapeutics
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** EXPANDED_ACCESS
- **Status:** NO_LONGER_AVAILABLE
- **Start date:** —
- **Primary completion:** —
- **Final completion:** —
- **Target enrollment:** — (—)
- **Last updated:** 2024-01-23


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01370447

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01370447, "EPI-743 for Mitochondrial Respiratory Chain Diseases". Retrieved via AI Analytics 2026-06-22 from https://api.ai-analytics.org/clinical/NCT01370447. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*