Study of Triheptanoin for Treatment of Long-Chain Fatty Acid Oxidation Disorder
Conditions
- Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency
- Carnitine Palmitoyltransferase 2 (CPT2) Deficiency
- Mitochondrial Trifunctional Protein (TFP) Deficiency
- Long-chain 3 hydroxyacylCoA Dehydrogenase (LCHAD) Deficiency
Interventions
Sponsor
Oregon Health and Science University
Collaborators