# A Phase I/II Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC

> **NCT01395641** · PHASE1,PHASE2 · COMPLETED · sponsor: **National Taiwan University Hospital** · enrollment: 10 (actual)

## Conditions studied

- Aromatic L-amino Acid Decarboxylase (AADC) Deficiency

## Interventions

- **DRUG:** gene therapy

## Key facts

- **NCT ID:** NCT01395641
- **Lead sponsor:** National Taiwan University Hospital
- **Sponsor class:** OTHER
- **Phase:** PHASE1,PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2014-10-22
- **Primary completion:** 2020-12-18
- **Final completion:** 2022-03-07
- **Target enrollment:** 10 (ACTUAL)
- **Last updated:** 2023-02-10

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01395641

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01395641, "A Phase I/II Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC". Retrieved via AI Analytics 2026-06-23 from https://api.ai-analytics.org/clinical/NCT01395641. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*