Efficacy Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy Patients
NCT01396239
·
clinicaltrials.gov ↗
PHASE2
Phase
COMPLETED
Status
12
Enrollment
INDUSTRY
Sponsor class
Conditions
Duchenne Muscular Dystrophy
Interventions
DRUG:
AVI-4658 (Eteplirsen)
OTHER:
Placebo
Sponsor
Sarepta Therapeutics, Inc.