# Gene Therapy for X-linked Severe Combined Immunodeficiency

> **NCT01410019** · PHASE1,PHASE2 · COMPLETED · sponsor: **Assistance Publique - Hôpitaux de Paris** · enrollment: 5 (actual)

## Conditions studied

- X-linked Severe Combined Immunodeficiency

## Interventions

- **OTHER:** Gene transfer

## Key facts

- **NCT ID:** NCT01410019
- **Lead sponsor:** Assistance Publique - Hôpitaux de Paris
- **Sponsor class:** OTHER
- **Phase:** PHASE1,PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2010-12
- **Primary completion:** 2015-06-16
- **Final completion:** 2015-06-16
- **Target enrollment:** 5 (ACTUAL)
- **Last updated:** 2026-03-11


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01410019

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01410019, "Gene Therapy for X-linked Severe Combined Immunodeficiency". Retrieved via AI Analytics 2026-05-28 from https://api.ai-analytics.org/clinical/NCT01410019. Licensed CC0.

---

*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
