# Pilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer for the Wiskott-Aldrich Syndrome

> **NCT01410825** · PHASE1,PHASE2 · COMPLETED · sponsor: **David Williams** · enrollment: 5 (actual)

## Conditions studied

- Wiskott-Aldrich Syndrome

## Interventions

- **BIOLOGICAL:** Retrovirus-mediated gene transfer

## Key facts

- **NCT ID:** NCT01410825
- **Lead sponsor:** David Williams
- **Sponsor class:** OTHER
- **Phase:** PHASE1,PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2011-07
- **Primary completion:** 2024-09
- **Final completion:** 2024-09
- **Target enrollment:** 5 (ACTUAL)
- **Last updated:** 2025-08-14


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01410825

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01410825, "Pilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer for the Wiskott-Aldrich Syndrome". Retrieved via AI Analytics 2026-06-02 from https://api.ai-analytics.org/clinical/NCT01410825. Licensed CC0.

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