# Observational Study for Subjects With Pompe Disease Undergoing Immune Modulation Therapies

> **NCT01451879** · — · COMPLETED · sponsor: **University of Florida** · enrollment: 11 (actual)

## Conditions studied

- Pompe Disease

## Interventions

- **DRUG:** Rituximab
- **DRUG:** Miglustat

## Key facts

- **NCT ID:** NCT01451879
- **Lead sponsor:** University of Florida
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2008-10
- **Primary completion:** 2017-10
- **Final completion:** 2017-10
- **Target enrollment:** 11 (ACTUAL)
- **Last updated:** 2017-12-08


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01451879

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01451879, "Observational Study for Subjects With Pompe Disease Undergoing Immune Modulation Therapies". Retrieved via AI Analytics 2026-06-08 from https://api.ai-analytics.org/clinical/NCT01451879. Licensed CC0.

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