# Safety and Efficacy Study of Sotatercept in Adults With Transfusion Dependent Diamond Blackfan Anemia

> **NCT01464164** · PHASE1,PHASE2 · TERMINATED · sponsor: **Northwell Health** · enrollment: 19 (actual)

## Conditions studied

- Diamond Blackfan Anemia

## Interventions

- **DRUG:** Sotatercept
- **DRUG:** Sotatercept with prednisone boost

## Key facts

- **NCT ID:** NCT01464164
- **Lead sponsor:** Northwell Health
- **Sponsor class:** OTHER
- **Phase:** PHASE1,PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** TERMINATED
- **Start date:** 2012-01
- **Primary completion:** 2021-04-13
- **Final completion:** 2021-04-13
- **Target enrollment:** 19 (ACTUAL)
- **Why stopped:** Supporter terminated the study due to no active patients (secondary to travel restrictions due to COVID).
- **Last updated:** 2023-03-17


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01464164

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01464164, "Safety and Efficacy Study of Sotatercept in Adults With Transfusion Dependent Diamond Blackfan Anemia". Retrieved via AI Analytics 2026-06-11 from https://api.ai-analytics.org/clinical/NCT01464164. Licensed CC0.

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