Intracerebral Gene Therapy for Sanfilippo Type A Syndrome
NCT01474343
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
COMPLETED
Status
4
Enrollment
INDUSTRY
Sponsor class
Conditions
Mucopolysaccharidosis Type III A
Sanfilippo Disease Type A
Interventions
GENETIC:
SAF-301
Sponsor
LYSOGENE