# Gene Transfer for X-Linked Severe Combined Immunodeficiency in Newly Diagnosed Infants

> **NCT01512888** · PHASE1,PHASE2 · SUSPENDED · sponsor: **St. Jude Children's Research Hospital** · enrollment: 28 (estimated)

## Conditions studied

- Severe Combined Immunodeficiency Disease, X-linked

## Interventions

- **GENETIC:** CL20-i4-EF1α-hγc-OPT
- **DRUG:** Busulfan
- **DEVICE:** CliniMacs

## Key facts

- **NCT ID:** NCT01512888
- **Lead sponsor:** St. Jude Children's Research Hospital
- **Sponsor class:** OTHER
- **Phase:** PHASE1,PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** SUSPENDED
- **Start date:** 2016-08-17
- **Primary completion:** 2026-08
- **Final completion:** 2034-08
- **Target enrollment:** 28 (ESTIMATED)
- **Why stopped:** voluntary hold
- **Last updated:** 2025-11-10

## Collaborators

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## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01512888

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01512888, "Gene Transfer for X-Linked Severe Combined Immunodeficiency in Newly Diagnosed Infants". Retrieved via AI Analytics 2026-06-25 from https://api.ai-analytics.org/clinical/NCT01512888. Licensed CC0.

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