Gene Therapy for Wiskott-Aldrich Syndrome
NCT01515462
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
COMPLETED
Status
8
Enrollment
OTHER
Sponsor class
Conditions
Wiskott-Aldrich Syndrome (WAS)
Interventions
GENETIC:
TLT003
Sponsor
Fondazione Telethon
Collaborators
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