# Gene Therapy for Wiskott-Aldrich Syndrome

> **NCT01515462** · PHASE1,PHASE2 · COMPLETED · sponsor: **Fondazione Telethon** · enrollment: 8 (actual)

## Conditions studied

- Wiskott-Aldrich Syndrome (WAS)

## Interventions

- **GENETIC:** TLT003

## Key facts

- **NCT ID:** NCT01515462
- **Lead sponsor:** Fondazione Telethon
- **Sponsor class:** OTHER
- **Phase:** PHASE1,PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2010-04-20
- **Primary completion:** 2023-10-04
- **Final completion:** 2023-10-04
- **Target enrollment:** 8 (ACTUAL)
- **Last updated:** 2025-04-04

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01515462

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01515462, "Gene Therapy for Wiskott-Aldrich Syndrome". Retrieved via AI Analytics 2026-06-23 from https://api.ai-analytics.org/clinical/NCT01515462. Licensed CC0.

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