# Follistatin Gene Transfer to Patients With Becker Muscular Dystrophy and Sporadic Inclusion Body Myositis

> **NCT01519349** · PHASE1 · COMPLETED · sponsor: **Nationwide Children's Hospital** · enrollment: 15 (actual)

## Conditions studied

- Becker Muscular Dystrophy
- Sporadic Inclusion Body Myositis

## Interventions

- **BIOLOGICAL:** rAAV1.CMV.huFollistatin344

## Key facts

- **NCT ID:** NCT01519349
- **Lead sponsor:** Nationwide Children's Hospital
- **Sponsor class:** OTHER
- **Phase:** PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2012-01
- **Primary completion:** 2017-10
- **Final completion:** 2017-10
- **Target enrollment:** 15 (ACTUAL)
- **Last updated:** 2023-10-02

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01519349

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01519349, "Follistatin Gene Transfer to Patients With Becker Muscular Dystrophy and Sporadic Inclusion Body Myositis". Retrieved via AI Analytics 2026-06-23 from https://api.ai-analytics.org/clinical/NCT01519349. Licensed CC0.

---

*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*