Ph 1 Study of ADI PEG 20 in Pediatric Subjects Who Are Argininosuccinate Synthetase (ASS) Deficient
NCT01528384
·
clinicaltrials.gov ↗
PHASE1
Phase
COMPLETED
Status
8
Enrollment
INDUSTRY
Sponsor class
Conditions
Argininosuccinate Synthetase Deficient
Interventions
DRUG:
ADI-PEG 20
Sponsor
Polaris Group