# Phenylbutyrate Therapy for Maple Syrup Urine Disease

> **NCT01529060** · PHASE2,PHASE3 · COMPLETED · sponsor: **Brendan Lee** · enrollment: 20 (actual)

## Conditions studied

- Maple Syrup Urine Disease

## Interventions

- **DRUG:** Phenylbutyrate
- **DRUG:** Placebo powder

## Key facts

- **NCT ID:** NCT01529060
- **Lead sponsor:** Brendan Lee
- **Sponsor class:** OTHER
- **Phase:** PHASE2,PHASE3
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2013-02
- **Primary completion:** 2017-09-02
- **Final completion:** 2017-12
- **Target enrollment:** 20 (ACTUAL)
- **Last updated:** 2019-03-19


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01529060

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01529060, "Phenylbutyrate Therapy for Maple Syrup Urine Disease". Retrieved via AI Analytics 2026-06-02 from https://api.ai-analytics.org/clinical/NCT01529060. Licensed CC0.

---

*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*