Study of Ataluren for Previously Treated Participants With Nonsense Mutation Duchenne/Becker Muscular Dystrophy (nmDBMD) in Europe, Israel, Australia, and Canada

NCT01557400 · clinicaltrials.gov ↗
PHASE3
Phase
COMPLETED
Status
94
Enrollment
INDUSTRY
Sponsor class

Conditions

Interventions

Sponsor

PTC Therapeutics