Gene Therapy for Metachromatic Leukodystrophy (MLD)
NCT01560182
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
COMPLETED
Status
20
Enrollment
INDUSTRY
Sponsor class
Conditions
Lysosomal Storage Disease
Metachromatic Leukodystrophy
Interventions
GENETIC:
OTL-200 Gene Therapy
Sponsor
Orchard Therapeutics
Collaborators
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