# Long-term Outcome of N-Carbamylglutamate Treatment in Propionic Acidemia and Methylmalonic Acidemia

> **NCT01597440** · PHASE2 · TERMINATED · sponsor: **Mendel Tuchman** · enrollment: 1 (actual)

## Conditions studied

- Propionic Acidemia
- Methylmalonic Acidemia

## Interventions

- **DRUG:** N-carbamylglutamate
- **OTHER:** Standard of Care

## Key facts

- **NCT ID:** NCT01597440
- **Lead sponsor:** Mendel Tuchman
- **Sponsor class:** OTHER
- **Phase:** PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** TERMINATED
- **Start date:** 2012-09
- **Primary completion:** 2015-02
- **Final completion:** 2015-02
- **Target enrollment:** 1 (ACTUAL)
- **Why stopped:** insufficient enrollment
- **Last updated:** 2017-04-26

## Collaborators

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## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01597440

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01597440, "Long-term Outcome of N-Carbamylglutamate Treatment in Propionic Acidemia and Methylmalonic Acidemia". Retrieved via AI Analytics 2026-06-02 from https://api.ai-analytics.org/clinical/NCT01597440. Licensed CC0.

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