A Noninferiority Study of Alglucosidase Alfa Manufactured at the 160 L and 4000 L Scales in Treatment Naïve Patients With Infantile-Onset Pompe Disease

NCT01597596 · clinicaltrials.gov ↗

PHASE4

Phase

TERMINATED

Status

4

Enrollment

INDUSTRY

Sponsor class

Stopped Study was stopped due to approved label expansion of alglucosidase alfa.

Conditions

Pompe Disease (Infantile-Onset)
Glycogen Storage Disease Type II (GSD II)
Glycogenosis 2
Acid Maltase Deficiency

Interventions

BIOLOGICAL: alglucosidase alfa
BIOLOGICAL: alglucosidase alfa

Sponsor

Genzyme, a Sanofi Company