# A Multicenter, Multinational Clinical Assessment Study for Pediatric Patients With Achondroplasia

> **NCT01603095** · — · COMPLETED · sponsor: **BioMarin Pharmaceutical** · enrollment: 363 (actual)

## Conditions studied

- Achondroplasia

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT01603095
- **Lead sponsor:** BioMarin Pharmaceutical
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2012-04
- **Primary completion:** 2021-02
- **Final completion:** 2021-02
- **Target enrollment:** 363 (ACTUAL)
- **Last updated:** 2021-04-13


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01603095

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01603095, "A Multicenter, Multinational Clinical Assessment Study for Pediatric Patients With Achondroplasia". Retrieved via AI Analytics 2026-06-02 from https://api.ai-analytics.org/clinical/NCT01603095. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
