Hemophilia B Gene Therapy With AAV8 Vector
NCT01620801
·
clinicaltrials.gov ↗
PHASE1
Phase
TERMINATED
Status
4
Enrollment
INDUSTRY
Sponsor class
Conditions
Hemophilia B
Interventions
BIOLOGICAL:
AAV8-hFIX19
Sponsor
Spark Therapeutics, Inc.
Collaborators
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