# Lysosomal Acid Lipase (LAL) Deficiency Registry

> **NCT01633489** · — · RECRUITING · sponsor: **Alexion Pharmaceuticals, Inc.** · enrollment: 300 (estimated)

## Conditions studied

- Lysosomal Acid Lipase Deficiency
- Cholesterol Ester Storage Disease
- Wolman Disease
- Acid Cholesteryl Ester Hydrolase Deficiency, Type 2
- Acid Lipase Deficiency
- LIPA Deficiency
- LAL-Deficiency

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT01633489
- **Lead sponsor:** Alexion Pharmaceuticals, Inc.
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** RECRUITING
- **Start date:** 2013-05-30
- **Primary completion:** 2029-08-30
- **Final completion:** 2029-08-30
- **Target enrollment:** 300 (ESTIMATED)
- **Last updated:** 2026-03-06


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01633489

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01633489, "Lysosomal Acid Lipase (LAL) Deficiency Registry". Retrieved via AI Analytics 2026-05-27 from https://api.ai-analytics.org/clinical/NCT01633489. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*