# Short and Long Term Treatment With 4-AP in Ambulatory SMA Patients

> **NCT01645787** · PHASE2,PHASE3 · COMPLETED · sponsor: **Columbia University** · enrollment: 11 (actual)

## Conditions studied

- Spinal Muscular Atrophy

## Interventions

- **DRUG:** 4-aminopyridine
- **DRUG:** Placebo

## Key facts

- **NCT ID:** NCT01645787
- **Lead sponsor:** Columbia University
- **Sponsor class:** OTHER
- **Phase:** PHASE2,PHASE3
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2012-06-01
- **Primary completion:** 2015-09
- **Final completion:** 2015-09
- **Target enrollment:** 11 (ACTUAL)
- **Last updated:** 2024-09-03

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01645787

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01645787, "Short and Long Term Treatment With 4-AP in Ambulatory SMA Patients". Retrieved via AI Analytics 2026-05-25 from https://api.ai-analytics.org/clinical/NCT01645787. Licensed CC0.

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