Efficacy and Safety Study of BMN 110 for Morquio A Syndrome Patients Who Have Limited Ambulation
NCT01697319
·
clinicaltrials.gov ↗
PHASE2
Phase
TERMINATED
Status
16
Enrollment
INDUSTRY
Sponsor class
Conditions
Mucopolysaccharidosis IVA
Morquio A Syndrome
MPS IVA
Interventions
DRUG:
BMN 110
Sponsor
BioMarin Pharmaceutical