Efficacy and Safety of Inotersen in Familial Amyloid Polyneuropathy
NCT01737398
·
clinicaltrials.gov ↗
PHASE2,PHASE3
Phase
COMPLETED
Status
173
Enrollment
INDUSTRY
Sponsor class
Conditions
FAP
Familial Amyloid Polyneuropathy
TTR
Transthyretin
Amyloidosis
Interventions
DRUG:
Inotersen
DRUG:
Placebo
Sponsor
Ionis Pharmaceuticals, Inc.