# Gene Therapy for Tay-Sachs Disease

> **NCT01869270** · — · COMPLETED · sponsor: **University of Minnesota** · enrollment: 4 (actual)

## Conditions studied

- Tay Sachs Disease
- Sandhoff Disease
- Late Onset Tay Sachs Disease

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT01869270
- **Lead sponsor:** University of Minnesota
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2010-12
- **Primary completion:** 2014-07
- **Final completion:** 2014-08
- **Target enrollment:** 4 (ACTUAL)
- **Last updated:** 2014-12-04

## Collaborators

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## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01869270

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01869270, "Gene Therapy for Tay-Sachs Disease". Retrieved via AI Analytics 2026-06-04 from https://api.ai-analytics.org/clinical/NCT01869270. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
