Use of Ravicti™ in Patients With MCAD Deficiency With the 985A>G (K304E) Mutation

NCT01881984 · clinicaltrials.gov ↗

PHASE1

Phase

COMPLETED

Status

4

Enrollment

OTHER

Sponsor class

Conditions

Medium-chain Acyl-CoA Dehydrogenase (MCAD) Deficiency

Interventions

DRUG: Ravicti

Sponsor

University of Pittsburgh

Collaborators

[object Object]