Lysosomal Storage Disease: Health, Development, and Functional Outcome Surveillance in Preschool Children
Conditions
- Mucopolysaccharidosis Type I (MPS I)
- Mucopolysaccharidosis Type II (MPS II)
- Mucopolysaccharidosis Type III (MPS III)
- Mucopolysaccharidosis Type VI (MPS VI)
- Krabbe Disease
Sponsor
University of Chicago
Collaborators
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