# Natural History Study of Children With Metachromatic Leukodystrophy

> **NCT01963650** · — · TERMINATED · sponsor: **Shire** · enrollment: 1 (actual)

## Conditions studied

- Lipid Metabolism Disorders
- Metachromatic Leukodystrophy (MLD)
- Nervous System Diseases
- Brain Diseases
- Central Nervous System Diseases
- Demyelinating Diseases
- Metabolism, Inborn Errors
- Genetic Diseases, Inborn
- Sphingolipidoses
- Hereditary Central Nervous System Demyelinating Diseases
- Metabolic Inborn Brain Diseases
- Lysosomal Storage Diseases
- Metabolic Diseases
- Sulfatidosis

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT01963650
- **Lead sponsor:** Shire
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** TERMINATED
- **Start date:** 2015-11-02
- **Primary completion:** 2016-04-08
- **Final completion:** 2016-04-08
- **Target enrollment:** 1 (ACTUAL)
- **Why stopped:** Enrollment issues
- **Last updated:** 2021-03-17


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01963650

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01963650, "Natural History Study of Children With Metachromatic Leukodystrophy". Retrieved via AI Analytics 2026-06-02 from https://api.ai-analytics.org/clinical/NCT01963650. Licensed CC0.

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