Safety Tolerability and Efficacy Study of Cabaletta to Treat Oculopharyngeal Muscular Dystrophy (OPMD) Patients
NCT02015481
·
clinicaltrials.gov ↗
PHASE2
Phase
COMPLETED
Status
25
Enrollment
INDUSTRY
Sponsor class
Conditions
Oculopharyngeal Muscular Dystrophy
Interventions
DRUG:
Cabaletta
Sponsor
Bioblast Pharma Ltd.