Phase 2 Clinical Trial of SGS-742 Therapy in Succinic Semialdehyde Dehydrogenase Deficiency
NCT02019667
·
clinicaltrials.gov ↗
PHASE2
Phase
COMPLETED
Status
19
Enrollment
NIH
Sponsor class
Conditions
Metabolic Disease
Seizures
Interventions
DRUG:
SGS-742
DRUG:
Placebo
Sponsor
National Institute of Neurological Disorders and Stroke (NINDS)