Treatment of SCID Due to ADA Deficiency With Autologous Transplantation of Cord Blood or Hematopoietic CD 34+ Cells After Addition of a Normal Human ADA cDNA by the EFS-ADA Lentiviral Vector
Conditions
- Adenosine Deaminase Deficiency
- ADA-SCID
Interventions
- GENETIC: Lentiviral Gene Transfer
Sponsor
National Human Genome Research Institute (NHGRI)
Collaborators
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