Synergistic Enteral Regimen for Treatment of the Gangliosidoses
Stopped Efficacy
Conditions
- GM1 Gangliosidoses
- GM2 Gangliosidoses
- Tay-Sachs Disease
- Sandhoff Disease
Interventions
- DRUG: miglustat
- OTHER: Ketogenic Diet
Sponsor
University of Minnesota
Collaborators
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