Safety & Efficacy Study of ORGN001 (Formerly ALXN1101) in Pediatric Patients With MoCD Type A Currently Treated With rcPMP

NCT02047461 · clinicaltrials.gov ↗

PHASE2

Phase

COMPLETED

Status

8

Enrollment

INDUSTRY

Sponsor class

Conditions

Molybdenum Cofactor Deficiency, Type A

Interventions

DRUG: ORGN001 (formerly ALXN1101)

Sponsor

Origin Biosciences