Safety Evaluation of Gene Therapy in Leber Hereditary Optic Neuropathy (LHON) Patients
NCT02064569
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
COMPLETED
Status
19
Enrollment
INDUSTRY
Sponsor class
Conditions
Leber Hereditary Optic Neuropathy
Interventions
GENETIC:
GS010
Sponsor
GenSight Biologics