Safety Study of Gene Modified Donor T-cells Following TCRαβ+ Depleted Stem Cell Transplant
Stopped Sponsor decision
Conditions
- Acute Lymphoblastic Leukemia
- Leukemia, Acute Myeloid (AML), Child
- Lymphoma, Non-Hodgkin
- Myelodysplastic Syndrome
- Primary Immunodeficiency
- Anemia, Aplastic
- Osteopetrosis
- Hemoglobinopathies
- Cytopenia
- Fanconi Anemia
- Diamond Blackfan Anemia
- Thalassemia
- Anemia, Sickle Cell
Interventions
- BIOLOGICAL: BPX-501 T cells
- DRUG: Rimiducid
Sponsor
Bellicum Pharmaceuticals