Gene Transfer Clinical Trial for Spinal Muscular Atrophy Type 1
NCT02122952
·
clinicaltrials.gov ↗
PHASE1
Phase
COMPLETED
Status
15
Enrollment
INDUSTRY
Sponsor class
Conditions
Spinal Muscular Atrophy 1
Interventions
BIOLOGICAL:
AVXS-101
Sponsor
Novartis Gene Therapies