Safety Dose Finding Study of ADVM-043 Gene Therapy to Treat Alpha-1 Antitrypsin (A1AT) Deficiency
NCT02168686
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
COMPLETED
Status
6
Enrollment
INDUSTRY
Sponsor class
Conditions
Alpha 1-Antitrypsin Deficiency
Interventions
GENETIC:
ADVM-043
Sponsor
Adverum Biotechnologies, Inc.