Extension Study Assessing Long Term Safety and Efficacy of IONIS-TTR Rx in Familial Amyloid Polyneuropathy (FAP)
NCT02175004
·
clinicaltrials.gov ↗
PHASE3
Phase
COMPLETED
Status
135
Enrollment
INDUSTRY
Sponsor class
Conditions
FAP
Familial Amyloid Polyneuropathy
TTR
Transthyretin
Amyloidosis
Interventions
DRUG:
Inotersen
Sponsor
Ionis Pharmaceuticals, Inc.