# A Pilot Study of Zavesca® in Patients With Pompe Disease and Infusion Associated Reaction

> **NCT02185651** · PHASE1 · TERMINATED · sponsor: **University of Florida** · enrollment: 2 (actual)

## Conditions studied

- Pompe Disease
- Hypersensitivity Reaction

## Interventions

- **DRUG:** Zavesca® Prescription

## Key facts

- **NCT ID:** NCT02185651
- **Lead sponsor:** University of Florida
- **Sponsor class:** OTHER
- **Phase:** PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** TERMINATED
- **Start date:** 2016-10
- **Primary completion:** 2018-07
- **Final completion:** 2018-07
- **Target enrollment:** 2 (ACTUAL)
- **Why stopped:** Participants not interested in enrolling.
- **Last updated:** 2018-12-05

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT02185651

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT02185651, "A Pilot Study of Zavesca® in Patients With Pompe Disease and Infusion Associated Reaction". Retrieved via AI Analytics 2026-06-08 from https://api.ai-analytics.org/clinical/NCT02185651. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
