Clinical Study In Infants With Rapidly Progressive Lysosomal Acid Lipase Deficiency

NCT02193867 · clinicaltrials.gov ↗

PHASE2

Phase

TERMINATED

Status

10

Enrollment

INDUSTRY

Sponsor class

Conditions

Lysosomal Acid Lipase Deficiency

Interventions

DRUG: Sebelipase Alfa

Sponsor

Alexion Pharmaceuticals, Inc.