# Clinical Study In Infants With Rapidly Progressive Lysosomal Acid Lipase Deficiency

> **NCT02193867** · PHASE2 · TERMINATED · sponsor: **Alexion Pharmaceuticals, Inc.** · enrollment: 10 (actual)

## Conditions studied

- Lysosomal Acid Lipase Deficiency

## Interventions

- **DRUG:** Sebelipase Alfa

## Key facts

- **NCT ID:** NCT02193867
- **Lead sponsor:** Alexion Pharmaceuticals, Inc.
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** TERMINATED
- **Start date:** 2014-06-06
- **Primary completion:** 2018-10-30
- **Final completion:** 2018-10-30
- **Target enrollment:** 10 (ACTUAL)
- **Last updated:** 2019-11-18


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT02193867

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT02193867, "Clinical Study In Infants With Rapidly Progressive Lysosomal Acid Lipase Deficiency". Retrieved via AI Analytics 2026-06-24 from https://api.ai-analytics.org/clinical/NCT02193867. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*