Triheptanoin Treatment Trial for Patients With Long-chain Fatty Acid Beta-oxidation Defects
Stopped IMP management difficulties
Conditions
- Long-chain Fatty Acid Transport Deficiency
Interventions
- DRUG: Triheptanoin (SpezialölÒ 107®)
- DIETARY_SUPPLEMENT: MCT (Medium-Chain Triglycerides)
Sponsor
Maria Luz Couce Pico
Collaborators