Observational Study to Evaluate Allogeneic HSCT Outcomes for Cerebral Adrenoleukodystrophy (CALD)
Stopped Sufficient enrollment for Month 24 safety and efficacy endpoints
Conditions
- X-Linked Adrenoleukodystrophy (X-ALD)
- Cerebral Adrenoleukodystrophy (CALD)
- Adrenoleukodystrophy (ALD)
Interventions
Sponsor
Genetix Biotherapeutics Inc.